An der Klinik für Pädiatrische Onkologie, Hämatologie und Immunologie des Universitätsklinikums Heidelbergs ist ab sofort die Behandlung einer bestimmten Form der Erbkrankheit Thalassämie, der seltenen transfusionsabhängigen β-Thalassämie (TDT), mit einer neuen Gentherapie möglich. „Diese Form der Thalassämie stellt eine enorme Belastung der Betroffenen dar und kann deren Lebenserwartung deutlich reduzieren", sagt Professor Andreas Kulozik, Ärztlicher Direktor nci Owxcsb mkj Dikkle pyd bakqgacnjr Khbivfocxt ypi HjXC (Mech-Ipisonghhjkhvheigo Vyzadyewjx).
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